Gene therapy in Glycogen Storage Disorders
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Innhold levert av JIMD Podcasts and Journal of Inherited Metabolic Disease. Alt podcastinnhold, inkludert episoder, grafikk og podcastbeskrivelser, lastes opp og leveres direkte av JIMD Podcasts and Journal of Inherited Metabolic Disease eller deres podcastplattformpartner. Hvis du tror at noen bruker det opphavsrettsbeskyttede verket ditt uten din tillatelse, kan du følge prosessen skissert her https://no.player.fm/legal.
Dr Dwight Koeberl joins the podcast to provide some background to gene therapies in Glycogen Storage Disorders, hi-light some ongoing studies and explain why we owe at least some of our knowledge to a menagerie of animal models. Gene therapy for glycogen storage diseases Dwight D. Koeberl, et al https://doi.org/10.1002/jimd.12654
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